Sessions on Personalized Medicine at the 2015 Joint Statistical Meetings

By Steve Pierson posted 06-15-2015 09:07

  

As I was going through the 2015 JSM Online Program, I was struck by the number of sessions related to personalized medicine (perhaps confirmation bias from the new ASA one-pager to promote statistics and statisticians in the Precision Medicine Initiative.) Below are just some I could identify by using the great search feature of the online program but I hope you'll spend more time using it to identify precision medicine talks. I also hope you'll let me know of any I missed.

The first list are sessions where "Personalized" appears in the title and includes an Introductory Overview Lecture by Erica Moodie, Michael Kosorok, and Eric Laber; the Medallion Lecture by Michael Kosorok; and the Wald Lectures by Susan Murphy.

Below the first list are talk titled with "personalized" in the abstract. I've also included talks with key words associated with or related to precision medicine (I did not de-duplicate these):

See also these keyword searches: biomarker (87 results); dynamic treatment regime (16 results); next generation sequencing (8 results). And feel free to suggest other keywords for precision medicine to me. 

See also, Big Data Sessions at the 2015 Joint Statistical Meetings, and coming soon, Neuroscience talks at JSM.

I'm also aware of several statistics-intensive sessions on the topic at other conferences. For example: 

 See other ASA Science Policy blog entries. For ASA science policy updates, follow @ASA_SciPol on Twitter.

 

Personalized Medicine Sessions

25 Recent Development in Personalized Medicine Sun, 8/9 2:00 PM to 3:50 PM
Room: CC-616
46 Introductory Overview Lecture: Personalized Medicine Sun, 8/9 4:00 PM to 5:50 PM
Room: CC-4C2
383 
 Closing the Research Practice Gap in Personalized Medicine 
Roundtable with Eric Laber, North Carolina State University
Tues, 8/11 12:30 PM to 1:50 PM
CC- Ballroom 6E   
393 Medallion Lecture III: Recent Developments in Machine Learning for Personalized Medicine Tue, 8/11 2:00 PM to 3:50 PM
Room: CC- Ballroom 6E
452 Wald Lecture ISequential Decision-Making and Personalized Treatment: The Future Is Now! Tue, 8/11 4:00 PM to 5:50 PM
Room: CC- Ballroom 6E
508 Wald Lecture II Offline Data Analysis Methods and Learning Algorithms for Constructing Mobile Treatment Policies  Wed, 8/12 10:30 AM to 12:20 PM
Room: CC- Ballroom 6E
663 Wald Lecture III Continual, Online Learning in Sequential Decision-Making Thu, 8/13 10:30 AM to 12:20 PM
Room: CC-4C

 

Talks with "Personalized" in the abstract

Sunday, 08/09/2015
An Actor-Critic Contextual Bandit Algorithm for Personalized Interventions Using Mobile Devices 
Huitian Lei, University of Michigan; Ambuj Tewari, University of Michigan; Susan A. Murphy, University of Michigan 
2:20 PM 

A Predictive Biomarker Model for Subgroup Selection 
Yu-Chuan Chen, FDA/NCTR; James J. Chen, FDA/NCTR 
2:35 PM 

Efficient Augmentation and Relaxation Learning for Treatment Regimes Using Observational Data 
Yingqi Zhao, University of Wisconsin - Madison; Eric Laber, North Carolina State University; Sumona Saha, University of Wisconsin - Madison 
4:45 PM 

Monday, 08/10/2015
Personalized Plans with Multiple Treatments 
Chathura Siriwardhana, University of Louisville; Meng Zhao, Mississippi State University; Somnath Datta, University of Louisville; Karunarathna Kulasekera, University of Louisville 


Personalized Evaluation of Biomarker Value in Risk Prediction and Treatment Selection: A Cost-Benefit Perspective 
Ying Huang, Fred Hutchinson Cancer Research Center; Eric Laber, North Carolina State University 
10:35 AM 

Prognostic and Predictive Values and Statistical Interactions in the Era of Personalized Medicine 
Jaya M. Satagopan, Memorial Sloan Kettering Cancer Center; Alexia Iasonos, Memorial Sloan Kettering Cancer Center; Qin Zhou, Memorial Sloan Kettering Cancer Center 
11:25 AM 

Modeling Placebo Response Using Multiple Functional Predictors 
Thaddeus Tarpey, Wright State University; Eva Petkova, New York University School of Medicine; R. Todd Ogden, Columbia University; Adam Ciarleglio, New York University; Bei Jiang, Columbia University/New York University 
2:05 PM 

Assessing Instructional Modalities: Individualized Treatment Effects for Personalized Learning 
Richard Levine, San Diego State University 
3:05 PM 

Tuesday, 08/11/2015
A Novel Method of Subgroup Identification by Using Virtual Twins and GUIDE (VG) for Development of Personalized Medicines 
Jia Jia; Qi Tang, AbbVie; Wangang Xie, AbbVie; Richard Rode, AbbVie 


A Localized Prediction Algorithm for Personalized Trauma Care 
Sara Moore; Alan Hubbard, UC Berkeley; Mitchell J. Cohen, UC San Francisco 


A Localized Prediction Algorithm for Personalized Trauma Care 
Sara Moore; Alan Hubbard, UC Berkeley; Mitchell J. Cohen, UC San Francisco 
9:05 AM 

Some Statistical Method in Bridging Efficacy Studies for Companion Diagnostic Tests 
Xiao-Hua Zhou, University of Washington 
10:35 AM 

Discovery of Principles of Nature from Matrix and Tensor Modeling of Large-Scale Molecular Biological Data 
Orly Alter, University of Utah 
10:35 AM 

Nonparametric Generated Effect Modifiers for Placebo Response 
Eva Petkova, New York University School of Medicine; Thaddeus Tarpey, Wright State University; Adam Ciarleglio, New York University; Bei Jiang, New York University School of Medicine; R. Todd Ogden, Columbia University; Zhe Su, New York University 
10:35 AM 

There's Personalized Medicine. Why Not Personalized Inference? 
Xiao-Li Meng, Harvard University; Keli Liu, Stanford University 
11:00 AM 

Medallion Lecture: Recent Developments in Machine Learning for Personalized Medicine 
Michael Kosorok, The University of North Carolina at Chapel Hill 
2:05 PM 

Evaluation of Biomarkers for Treatment Selection Using Individual Participant Data Meta-Analysis 
Chaeryon Kang, University of Pittsburgh; Holly Janes, Fred Hutchinson Cancer Research Center 
2:05 PM 

Adaptive Enrichment Designs with Population Selection Based on an Ordinal Biomarker 
Michael Rosenblum, Johns Hopkins Bloomberg School of Public Health; Yu Du, The Johns Hopkins University; Aaron Fisher, The Johns Hopkins University; Tianchen Qian 
2:05 PM 

Subgroup Mixable Inference with Time-to-Event Outcomes in Personalized Medicine Development 
Ying Ding, University of Pittsburgh 
2:50 PM 

Designing a Confirmatory Trial with a Continuous Biomarker Endpoint and an Undetermined Threshold Tested at Both the Interim and Final 
Adarsh Joshi, Gilead Sciences; Jenny Zhang, Gilead Sciences; Nusrat Rabbee, UC Berkeley; Liang Fang, Gilead Sciences 
3:05 PM 

Sequential Decision-Making and Personalized Treatment: The Future Is Now! 
Susan A. Murphy, University of Michigan 
4:05 PM 

Wednesday, 08/12/2015
Decision-Making in Post Clinical Trials 
Heping Zhang, Yale University 
9:00 AM 

Bias Correction in Subgroup Analysis with Survival Outcomes 
Lu Tian, Stanford University; LJ Wei, Harvard University; Fei Jiang, Harvard University 
9:25 AM 

Personalized Predictions Using Exogenous Covariates 
Jie Fan; J. Sunil Rao, University of Miami 
9:50 AM 

Issues That Arise During the FDA Review of Applications Containing Patient and Clinician Reported Outcomes 
Laura Lee Johnson, FDA; Scott Komo, FDA/CDER/OTS/OB/DBIV; Thomas Birkner, FDA/CDER/OTS/OB/DBI; LaRee Tracy, FDA/CDER/OTS/OB/DBIV; Stephen Wilson, FDA/CDER/OTS/OB/DBIII; Wen-Hung Chen, FDA/CDER/OND/SEALD; Martin Ho, FDA/CDRH 
10:35 AM 

Sequential Designs for Individualized Dosing in Phase I Cancer Clinical Trials 
Xuezhou Mao, Sanofi-Aventis U.S.; Ken Cheung, Columbia University 
11:25 AM 

Logical Inference on Efficacy in Subgroups and Their Combinations in Personalized Medicine 
Jason Hsu, The Ohio State University 
11:35 AM 

Composite Score-Based Decision Rule as a Predictive Signature for Patient Subgroup Identification 
Xin Huang; Yan Sun, AbbVie; Lu Tian, Stanford University; Viswanath Devanarayan, AbbVie 
11:50 AM 

Learning Optimal Personalized Treatment Rules Under Risk Constraint 
Yuanjia Wang, Columbia University; Haoda Fu, Eli Lilly and Company; Donglin Zeng, The University of North Carolina 
2:05 PM 

Algorithms for Prediction and Subgroup Formation in Personalized Medical Decision-Making 
Kelci Miclaus, SAS Institute; Richard Zink, SAS Institute; Russ C. Wolfinger, SAS Institute 
2:05 PM 

Thursday, 08/13/2015
Brain Imaging and Personalized Medicine in Psychiatry 
R. Todd Ogden, Columbia University; Adam Ciarleglio, New York University; Bei Jiang, Columbia University/New York University; Eva Petkova, New York University School of Medicine; Thaddeus Tarpey, Wright State University 
9:00 AM 

A Unified Family of Covariate-Adjusted Response-Adaptive Designs Based on Efficiency and Ethics 
Jianhua Hu, MD Anderson Cancer Center; Hongjian Zhu, The University of Texas School of Public Health; Feifang Hu, The George Washington University 
9:35 AM 

Interpretable Treatment Regimes 
Yichi Zhang, North Carolina State University; Eric Laber, North Carolina State University; Anastasios Tsiatis, North Carolina State University ; Marie Davidian, North Carolina State University 
11:50 AM 

 

Sessions or Talks with "Subgroup"

164 Subgroup Analyses: How Friendly Are They? Mon, 8/10 10:30 AM to 12:20 PM
Room: CC-3A
285 Key Subgroup Analysis Issues in Clinical Trials Tue, 8/11 8:30 AM to 10:20 AM
Room: CC-4C3
420 Statistical Methods in Genetics and Subgroup Identification Tue, 8/11 2:00 PM to 3:50 PM
Room: CC-611
Sunday, 08/09/2015
A Predictive Biomarker Model for Subgroup Selection 
Yu-Chuan Chen, FDA/NCTR; James J. Chen, FDA/NCTR 
2:35 PM 

Testing Multiple Endpoints in Multiple Prespecified Subgroups Using Group Sequential Procedures 
Christine Gause, Merck; Keaven Anderson, Merck 
3:20 PM 

Inference on Subgroups and All-Comers Cognizant of Logical Relationships Among Efficacy Parameters 
Szu-Yu Tang, Ventana Medical Systems, Inc.; Jason Hsu, The Ohio State University 
4:05 PM 

MOST: Multi-Stage Optimal Sequential Trial Design for Phase II Clinical Trials with Biomarker Subgroups 
Yong Zang, Florida Atlantic University 
5:20 PM 

Monday, 08/10/2015
A Comparison of Alternative Approaches to Analyzing Subgroup Differences in Survival After AIDS Diagnosis When the Proportional Hazards Assumption Does Not Hold 
Felicia Hardnett, CDC; Qian An, CDC; Xinjian Zhang, CDC 


Dunn Index Bootstrap (DIBS): A Procedure to Empirically Select a Cluster Analysis Method That Identifies Biologically and Clinically Relevant Molecular Subgroups 
Iwona Pawlikowska, St. Jude Children's Research Hospital; Zhifa Liu, St. Jude Children's Research Hospital; Arzu Onar-Thomas, St. Jude Children's Research Hospital; Stan Pounds, St. Jude Children's Research Hospital 


Identifying a Patient Subgroup with Differential Treatment Benefit 
David Prince, University of Washington; Susanne May, University of Washington; Scott Emerson, University of Washington; Michael LeBlanc, Fred Hutchinson Cancer Research Center; Erika Thommes, University of Washington 
9:50 AM 

Subgroup Analysis: Issues in FDA-Reviewed Clinical Trials 
Kathleen Fritsch, FDA 
10:35 AM 

A Comparison of Alternative Approaches to Analyzing Subgroup Differences in Survival After AIDS Diagnosis When the Proportional Hazards Assumption Does Not Hold 
Felicia Hardnett, CDC; Qian An, CDC; Xinjian Zhang, CDC 
10:55 AM 

Visualization Tools for Subgroup Analysis: Are We Using Them to Their Optimal Capacity? 
Vipin Arora, Eli Lilly and Company 
10:55 AM 

Dunn Index Bootstrap (DIBS): A Procedure to Empirically Select a Cluster Analysis Method That Identifies Biologically and Clinically Relevant Molecular Subgroups 
Iwona Pawlikowska, St. Jude Children's Research Hospital; Zhifa Liu, St. Jude Children's Research Hospital; Arzu Onar-Thomas, St. Jude Children's Research Hospital; Stan Pounds, St. Jude Children's Research Hospital 
11:15 AM 

Casting the Bones: The Worth and Potential Worthlessness of Subgroup Analyses 
Kevin Buhr, University of Wisconsin - Madison 
11:15 AM 

Subgroup Analysis Findings of Safety with No Statistical Power: What Do These Really Mean? 
Melvin Munsaka, Takeda Development Center Americas, Inc. 
11:35 AM 

Subgroup-Based Adaptive (SUBA) Designs for Sequential, Multiple Assignment, Randomized Trials 
Yanxun Xu, The University of Texas at Austin; Peter Mueller, The University of Texas at Austin; Peter F. Thall, MD Anderson Cancer Center 
11:50 AM 

Tuesday, 08/11/2015
Regularized Outcome Weighted Subgroup Identification for Differential Treatment Effects 
Yaoyao Xu, AbbVie; Menggang Yu, University of Wisconsin - Madison; Yingqi Zhao, University of Wisconsin - Madison; Quefeng Li, Princeton University; Sijian Wang, University of Wisconsin - Madison; Jun Shao, University of Wisconsin - Madison 


A Novel Method of Subgroup Identification by Using Virtual Twins and GUIDE (VG) for Development of Personalized Medicines 
Jia Jia; Qi Tang, AbbVie; Wangang Xie, AbbVie; Richard Rode, AbbVie 


Reducing Alpha Adjustment When Tests Are Structurally Correlated 
Jonathan Siegel, Bayer HealthCare Pharmaceuticals 


Generalized Error Rates for Subgroup Analyses 
Xiaolei Xun, Novartis; Frank Bretz, Novartis; Willi Maurer, Novartis 


Closing the Research Practice Gap in Personalized Medicine 
Eric Laber, North Carolina State University 


Do Subgroup Analyses Harm? Usually Not. Are They Helpful? It Depends. A Regulatory and Practical Review 
Christoph Muysers, Bayer HealthCare 
8:35 AM 

Multiple Testing in Clinical Trials: Some New Applications 
Yunzhi Lin, AbbVie; Kefei Zhou, Amgen; Jeetu Ganju, Hyperion Therapeutics 
8:35 AM 

Common Practices in Industry for Subgroups Identification and Analysis in Clinical Trials 
Cristiana Mayer, Janssen R&D/Johnson & Johnson 
8:55 AM 

Many Faces of Subgroup Analysis in Clinical Drug Development 
Ilya Lipkovich, Quintiles; Alex Dmitrienko, Quintiles 
9:15 AM 

Multiplicity and Subgroups in Benefit-Risk Assessment 
Jonathan Norton 
9:35 AM 

A Bayesian Credible Subgroups Approach to Identifying Patient Subgroups with Positive Treatment Effects 
Patrick M. Schnell, University of Minnesota; Qi Tang, AbbVie; Walt Offen, AbbVie; Bradley P. Carlin, University of Minnesota 
2:05 PM 

Subgroup Mixable Inference with Time-to-Event Outcomes in Personalized Medicine Development 
Ying Ding, University of Pittsburgh 
2:50 PM 

Designing a Confirmatory Trial with a Continuous Biomarker Endpoint and an Undetermined Threshold Tested at Both the Interim and Final 
Adarsh Joshi, Gilead Sciences; Jenny Zhang, Gilead Sciences; Nusrat Rabbee, UC Berkeley; Liang Fang, Gilead Sciences 
3:05 PM 

Change-Plane Analysis for Subgroup Identification and Sample Size Calculation 
Ailin Fan, North Carolina State University; Wenbin Lu, North Carolina State University; Rui Song, North Carolina State University 
3:20 PM 

Wednesday, 08/12/2015
Incorporating Historical Data in Bayesian Phase I Trial Design: Evaluating the Similarity in Dose-Toxicity Relationship Between Subgroups 
Kentaro Takeda, Astellas; Satoshi Morita, Kyoto University Graduate School of Medicine 
9:05 AM 

Bias Correction in Subgroup Analysis with Survival Outcomes 
Lu Tian, Stanford University; LJ Wei, Harvard University; Fei Jiang, Harvard University 
9:25 AM 

Logical Inference on Efficacy in Subgroups and Their Combinations in Personalized Medicine 
Jason Hsu, The Ohio State University 
11:35 AM 

Composite Score-Based Decision Rule as a Predictive Signature for Patient Subgroup Identification 
Xin Huang; Yan Sun, AbbVie; Lu Tian, Stanford University; Viswanath Devanarayan, AbbVie 
11:50 AM 

Thresholding of a Continuous Biomarker Based on a New Concept That Correctly Infers Efficacy in the Target Subgroup 
Yi Liu; Jason Hsu, The Ohio State University; Szu-Yu Tang, Ventana Medical Systems, Inc. 
11:55 AM 

Algorithms for Prediction and Subgroup Formation in Personalized Medical Decision-Making 
Kelci Miclaus, SAS Institute; Richard Zink, SAS Institute; Russ C. Wolfinger, SAS Institute 
2:05 PM 

Basket Trial Using Bayesian Hierarchical Models 
Zijiang Yang 
2:20 PM 

Generalization of Health Effects from Subgroups to Study Populations of Interest 
Amber J. Hackstadt, Social & Scientific Systems; Matthew D. Curry, Social & Scientific Systems; Lawrence S. Engel, The University of North Carolina at Chapel Hill; Richard K. Kwok, National Institute of Environmental Health Sciences; Dale P. Sandler, National Institute of Environmental Health Sciences 
3:20 PM 

Thursday, 08/13/2015
A Novel Approach in Subgroup Identification Using a Quantitative Benefit-Risk Index 
Ramin Arani, AstraZeneca; Ian Hirsch, AstraZeneca; Jonathan Norton, MedImmune; Christy Chuang-Stein, Pfizer Inc.; Weili He, Merck; Shihua Wen, AbbVie; Qi Jiang, Amgen 
8:35 AM 

Dose-Finding Using Hierarchical Modeling for Multiple Subgroups 
Kristen Cunanan, University of Minnesota; Joe Koopmeiners, University of Minnesota 
8:55 AM 

Treatment Response Subgroup Identification Using Penalized Regression Spline and Mixture Models 
Hongjie Zhu, Sanofi; Lin Wang, Sanofi; Lynn Wei, Sanofi; Hui Quan, Sanofi 
9:05 AM 

Identify Subset of Patients Benefiting from Treatment for Patients with Liver Cancer 
Yihuan Xu, Eli Lilly and Company; Yanzhi Hsu, Eli Lilly and Company; Ling Yang, Eli Lilly and Company 
9:15 AM 

Exchangeability and Nonexchangeability in Subgroup Analysis 
Margaret Gamalo-Siebers, FDA/CDER; Ram Tiwari, FDA/CDER/OT/OB 
9:35 AM 

Selection of Multiplicity Adjustment Strategy in Confirmatory Trials with a Targeted Subgroup 
Cheng Zheng, Novartis Pharmaceuticals; Zhichao Sun, University of Michigan; Kalyanee Appanna, Novartis Pharmaceuticals; Kaushal Mishra, Novartis Pharmaceuticals; Yong Zhang, Novartis Pharmaceuticals; Feng Tai, Novartis Pharmaceuticals 
12:05 PM 

Sessions or Talks with "Genome-Wide" 

Sunday, 08/09/2015
Integrative Genomic Analysis via Sparse Simultaneous Signal Detection 
Hongzhe Li, University of Pennsylvania 
2:05 PM 

Bayesian Hierarchical Variable Selection for Genome-Wide Association Studies 
Yize Zhao, SAMSI; Hongtu Zhu, The University of North Carolina at Chapel Hill; Zhaohua Lu, Penn State; Rebecca C. Knickmeyer, The University of North Carolina; Fei Zou, The University of North Carolina 
2:25 PM 

Monday, 08/10/2015
The Correction of Length-Bias in Gene Set Analysis for DNA Methylation Data 
Shaoyu Li, The University of North Carolina at Charlotte; Iwona Pawlikowska, St. Jude Children's Research Hospital; Tong Lin, St. Jude Children's Research Hospital 


Integrative Modeling of Multi-Track Hi-C Data for Genome-Scale Reconstruction of 3D Chromatin Structure 
Chenchen Zou, The Jackson Laboratory for Genomic Medicine; Yuping Zhang, University of Connecticut; Zhengqing Ouyang, The Jackson Laboratory for Genomic Medicine 


Optimal Multiple Testing with Prior Information 
Edgar Dobriban, Stanford University; Art Owen, Stanford University; Stuart Kim, Stanford University; Kristen Fortney, Stanford University 
8:35 AM 

Practical Methods for Privacy-Preserving Genome-Wide Association Study Data Sharing 
Fei Yu, Carnegie Mellon University; Zhanglong Ji, UC San Diego 
9:35 AM 

Semiparametric Mixed-Model Analysis for Nonlinear Gene-Environment Interactions in Genome-Wide Association Studies 
Zijian Huang, UC Riverside; Shujie Ma, UC Riverside 
12:05 PM 

Assessing the Impact of Genotype Imputation on Genome-Wide Meta-Analysis 
Elif Acar, University of Manitoba; Emmanuel Omondi, University of Basel 
3:05 PM 

Tuesday, 08/11/2015
Genome-Wide Haplotypic Testing in a Finnish Cohort Identifies a Novel Association with Low-Density Lipoprotein Cholesterol 
Qian Zhang, University of Washington; Sharon Browning, University of Washington; Brian Browning, University of Washington 


Analysis for Multiple Phenotypes in Genome-Wide Association Studies 
Xihong Lin, Harvard School of Public Health; Zhonghua Liu, Harvard University 
9:50 AM 

Genome-Wide Haplotypic Testing in a Finnish Cohort Identifies a Novel Association with Low-Density Lipoprotein Cholesterol 
Qian Zhang, University of Washington; Sharon Browning, University of Washington; Brian Browning, University of Washington 
10:55 AM 

Wednesday, 08/12/2015
Permutation-Based Genomewide Association Test for Case-Dependent Quantitative Trait 
Wei Xue, The University of North Carolina at Chapel Hill 


Detection of Shared Genetic Variants Between Complex Diseases While Preserving LD Structure 
Julie Kobie, University of Pennsylvania Perelman School of Medicine; Sihai Zhao, University of Illinois at Urbana-Champaign; Yun R. Li, Children's Hospital of Philadelphia; Hakon Hakonarson, Children's Hospital of Philadelphia; Hongzhe Li, University of Pennsylvania 
10:35 AM 

Testing for Gene-Environment Interactions Under Environment Misspecification 
Ryan Sun, Harvard University; Xihong Lin, Harvard School of Public Health 
11:35 AM 

Thursday, 08/13/2015
Group Association Test Using Hidden Markov Model 
Yichen Cheng, Fred Hutchinson Cancer Research Center; James Y. Dai, Fred Hutchinson Cancer Research Center; Charles Kooperberg, Fred Hutchinson Cancer Research Center 
8:35 AM 

Strategies on Genome-Wide Interaction Analysis Using Case-Parents Data 
Zhaoxia Yu, UC Irvine 
11:25 AM 

Model Selection in Genome-Wide Association Studies 
Kevin Keys, UCLA; Gary Chen, University of Southern California; Kenneth Lange, UCLA 
11:35 AM 

Annotation Regression of Genome-Wide Association Studies (ARoG) with an Application to Psychiatric Genomics Consortium Data 
Sunyoung Shin, University of Wisconsin; Sunduz Keles, University of Wisconsin 
12:05 PM 

Talks with the word "Targeted" in the abstract

Sunday, 08/09/2015
Position-Specific Artifact Removal for Targeted Next-Generation Sequencing--Based Somatic Mutation Detection 
John Kang 
4:35 PM 

Enrichment Design for Targeted Therapy 
Bo Yang, AbbVie Pharmaceutical Research & Development; Yijie Zhou, AbbVie; Lanju Zhang, AbbVie; Lu Cui, AbbVie 
4:45 PM 

Regulatory Challenges in Reviewing Targeted Therapy Trial 
Kun He, DBV/OB/CDER/FDA; Rajeshwari Sridhara, FDA 
5:05 PM 

MOST: Multi-Stage Optimal Sequential Trial Design for Phase II Clinical Trials with Biomarker Subgroups 
Yong Zang, Florida Atlantic University 
5:20 PM 

Comparison of a Targeted Maximum Likelihood Estimator to Other Estimation Techniques for the One-Year Risk of Recurrent MI Among New Users of High vs. Low Potency Statins 
Jonathan Todd, The University of North Carolina Gillings School of Global Public Health; Michele Jonsson Funk, The University of North Carolina Gillings School of Global Public Health; Alan Brookhart, The University of North Carolina at Chapel Hill 
5:25 PM 

Monday, 08/10/2015
Estimation of Dosage Frequency of Pre-Exposure Prophylaxis Needed to Protect Against HIV Infection 
Claire Ruberman 


Methods for Increasing Power in Vaccine Efficacy Trials 
David Benkeser; Peter B. Gilbert, Fred Hutchinson Cancer Research Center; Marco Carone, University of Washington 
8:55 AM 

Subgroup-Based Adaptive (SUBA) Designs for Sequential, Multiple Assignment, Randomized Trials 
Yanxun Xu, The University of Texas at Austin; Peter Mueller, The University of Texas at Austin; Peter F. Thall, MD Anderson Cancer Center 
11:50 AM 

Collaborative Targeted Maximum Likelihood Estimator (CTMLE) in Observational Studies 
Mark Johannes van der Laan, UC Berkeley; Sam Lendle, UC Berkeley; Sebastian Schneeweiss, Brigham and Women's Hospital 
2:25 PM 

Multistage Adaptive Biomarker-Directed Targeted Clinical Trial Design 
Zhong Gao, OBE/CBER/FDA; Ming Tan, Georgetown University; Anindya Roy, University of Maryland, Baltimore County 
3:05 PM 

Tuesday, 08/11/2015
Targeted Sampling, Mixed Mode, Incentives, and Paying for Completion: What Works for Reaching Hard-to-Survey Low-Income Households with Civil Legal Needs? 
Danna Moore, Washington State University Social & Economic Science Research Center; Arina Gertseva, Social & Economic Sciences Research Center; Nathan Palmer, Social & Economic Sciences Research Center 


Auto-Adaptive Alpha Allocation: A Strategy to Mitigate Risk on Study Assumptions 
Yue Shentu, Merck; Cong Chen, Merck Research Laboratories; Lei Pang, Merck 
2:25 PM 

Wednesday, 08/12/2015
Census Tract-Level Disparities: Examining Food Swamps and Food Deserts 
Lucy D'Agostino McGowan, Vanderbilt University; Alice Toll, Vanderbilt University 


Census Tract-Level Disparities: Examining Food Swamps and Food Deserts 
Lucy D'Agostino McGowan, Vanderbilt University; Alice Toll, Vanderbilt University 
8:40 AM 

Using Biomarkers for Better Decisions in Cancer Clinical Trials 
Yimei Li, University of Pennsylvania; Ming Wang, Penn State; Ken Cheung, Columbia University 
11:00 AM 

Thursday, 08/13/2015
Bayesian Dose-Finding Designs for Combination of Molecularly Targeted Agents Assuming Partial Stochastic Ordering 
Beibei Guo, Louisiana State University; Yisheng Li, MD Anderson Cancer Center 
10:55 AM 

Statistical Challenges in Oncology Clinical Trials in the Era of Targeted Therapy 
Rajeshwari Sridhara, FDA 
11:15 AM 

Selection of Multiplicity Adjustment Strategy in Confirmatory Trials with a Targeted Subgroup 
Cheng Zheng, Novartis Pharmaceuticals; Zhichao Sun, University of Michigan; Kalyanee Appanna, Novartis Pharmaceuticals; Kaushal Mishra, Novartis Pharmaceuticals; Yong Zhang, Novartis Pharmaceuticals; Feng Tai, Novartis Pharmaceuticals 
12:05 PM 

Keyword "Sequential Mutliple"

Monday, 08/10/2015
Set Valued Dynamic Treatment Regimes 
Tianshuang Wu, University of Michigan; William Pelham, Florida International University; Susan A. Murphy, University of Michigan 


Tuesday, 08/11/2015
Sequential Multiple Assignment Randomization Trials with EnRichment (SMARTer) Design 
Ying Liu, Columbia University; Yuanjia Wang, Columbia University; Donglin Zeng, The University of North Carolina 
2:45 PM 

Comparing Treatment Policies with Assistance from the Structural Nested Mean Model 
Xi Lu, University of Michigan; Kevin Lynch, University of Pennsylvania; David Oslin, University of Pennsylvania; Susan A. Murphy, University of Michigan 
3:05 PM 

Wednesday, 08/12/2015
Sequential Multiple Testing for Variable Selection to Control Error Rate 
Hailu Chen, UC Riverside; Cui Xinping, UC Riverside 
11:50 AM 

Thursday, 08/13/2015
Incorporating the SMART Design into Oncology: Overcoming Challenges to Reap the Benefits 
Kelley McLain Kidwell, University of Michigan 
11:35 AM 

 

 

 

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06-26-2015 09:59

Dr. Eric Laber will lead a roundtable discussion on "Closing the research-practice gap in personalized medicine" on Tuesday 8/11.